Nemzeti Népegészségügyi és Gyógyszerészeti Központ, 1097 Budapest Albert Flórián út,3/a fsz.
15
Irásbeli
1
3
2024-10-03 16:00:00
The course gives an overview of the field of human gene therapy. It covers the fundamentals of gene delivery into human cells, including non-viral and viral vectors and protocols. We will discuss the various gene therapy options for the treatment of malignant diseases with a special focus on clinical trials reaching clinical trial phase 4. The gene therapy treatment of inherited genetic diseases including severe combined immunodeficiency (SCID), spinal muscular atrophy (SMA), inherited retinal disease, etc. will be disputed as well. Finally, we intend to focus on protocols applied for vaccinations against various diseases including SARS2.
